UAE launches new initiative to test effectiveness of treatments for thalassemia

Asma Ahmed - | UAE

Health facilities in Abu Dhabi, overseen by the Abu Dhabi Department of Health, are leading efforts in clinical trials to evaluate new treatments for thalassemia.

Advancing Thalassemia Treatment in Abu Dhabi

Health facilities in Abu Dhabi, under the guidance of the Abu Dhabi Department of Health, are actively involved in conducting clinical trials to evaluate the safety and efficacy of new treatments for thalassemia. These efforts offer renewed hope for thalassemia patients in the UAE, with a particular focus on participation in global studies such as ENERGIZE and ENERGIZE-T, which are assessing the effectiveness of a novel drug named "Metapivat." The Emirates Thalassemia Society confirms that thalassemia centers across the UAE provide cutting-edge therapeutic technologies to patients of all nationalities, free of charge.

Global Trials and Hope for Patients

Dr. Khaled Musallam, head of the research department and founding director of the Rare Blood Disorders Research Center at Burjeel Holding and an honorary professor at Khalifa University and Weill Cornell Medical College in New York, underscores Abu Dhabi's pivotal role as a center for scientific research and advanced thalassemia treatments. The emirate actively participates in global clinical trials and conducts local studies aimed at enhancing patient care and understanding the unique clinical requirements of thalassemia patients in the UAE.

Thalassemia, characterized by genetic defects affecting hemoglobin production, necessitates lifelong management. Patients with the severe form, transfusion-dependent thalassemia (TDT), require regular blood transfusions to survive, which can lead to iron overload in organs like the heart and liver. Dr. Musallam highlights the challenges posed by current treatments and the potential of emerging therapies, including bone marrow transplants, which have shown promise in achieving long-term remission for some patients.

Abu Dhabi boasts advanced facilities capable of performing bone marrow transplants and other innovative treatments, such as gene therapy, which aims to correct or replace defective genes responsible for thalassemia. These treatments are part of global clinical trials that provide early access to state-of-the-art therapies for UAE patients, supported by the Department of Health in Abu Dhabi.

Dr. Muhammad Fahd Abdullah, a consultant specializing in pediatric hematology, oncology, and bone marrow transplantation at Burjeel Medical City, emphasizes the early onset of symptoms in children with moderate to severe thalassemia. Diagnosis involves comprehensive tests to assess red blood cell counts, abnormalities, and genetic markers. Treatment options vary depending on disease severity, with bone marrow transplantation offering curative potential in selected cases.

The Abu Dhabi Stem Cell Center plays a crucial role in raising awareness about thalassemia, a prevalent genetic disorder affecting millions worldwide. Through initiatives and collaborative efforts, including gene therapy and advanced bone marrow transplants, the center strives to advance treatment options and improve outcomes for thalassemia patients in Abu Dhabi and beyond.

Symptoms of thalassemia range from mild anemia in carriers to severe complications such as organ enlargement, frequent infections, and fatigue. Early detection through comprehensive screening programs is essential for managing the disease effectively and optimizing patient care.

Abu Dhabi's commitment to thalassemia research and treatment underscores its dedication to advancing healthcare and supporting patients with innovative therapies. By participating in global trials and implementing local initiatives, Abu Dhabi aims to alleviate the burden of thalassemia and enhance the quality of life for affected individuals across the UAE.

About Author

Asma Ahmed
Asma Ahmed
1648 Total posts

Read Also

UAE warn of fines of up to Dh100,000 for the unlawful use of prescribed medications

Authorities in the United Arab Emirates have issued a warning that individuals who illegally use authorized pharmaceuticals might face fines of up to 100,000 dirhams.

‏Urgent.. The Prime Minister announces the new ministers in the UAE government

Today, Sunday, Sheikh Mohammed bin Rashid Al Maktoum, Vice President of the UAE, Prime Minister and Ruler of Dubai, announced the new formation of the UAE government.

Mohre announces the facilitation of work permit procedures in the UAE when issued or cancelled

The Ministry of Human Resources and Emiratisation announced the facilitation of work permit procedures when issued or cancelled.

Dubai Airport announces new restrictions on passengers

Dubai Airport authorities announced some restrictions for non-travelers in July and August.

Companies in the UAE provide alternative systems for end-of-service compensation

Various alternate methods of end-of-service compensation are offered by businesses in the United Arab Emirates.

New important instructions for passengers traveling through Dubai airports

Travelers in a hurry to leave Dubai are advised to complete immigration 1.5 hours in advance of departure.

FTA announces the imposition of a fine of 10 thousand dirhams in the UAE due to taxes

It has been announced by the FTA that a fine of ten thousand dirhams will be imposed in the United Arab Emirates due to taxation.

The Meteorological Authority announces the date of rain in the UAE during the coming days and weeks

The dates of the upcoming rainy days and weeks in the Emirates are announced by the Meteorological Authority.

Mohre announces paid holiday for employees in the UAE

Mohre has stated that employees in the UAE will receive paid vacation time.

Expo Dubai gives families the chance to win a summer vacation in 7 destinations

During Expo Dubai, families have the opportunity to win a summer trip to one of seven different locations.

Dubai Mall Introduces Paid Parking from July 1 with Salik Boards Near Entrances

Boards displaying the distinctive grey and white Salik branding have recently appeared at various entrances of Dubai Mall, signaling the imminent introduction of paid parking for visitors.

The UAE authorities announced the evacuation of residents from a residential tower in Sharjah

It was stated by the authorities in the United Arab Emirates that the occupants of a residential tower in Sharjah would be evacuated.

Dubai announces plan to add 32 new metro stations by 2030

Dubai's Metro service is set to significantly expand in the coming years following the approval of a development plan by the emirate's Executive Council.

Dubai Targets $177bn FDI by 2033 with Major Metro Area Developments

Dubai has set an ambitious target to attract AED650 billion ($177 billion) in foreign direct investment (FDI) by 2033, supported by the Dubai Executive Council.

UAE announces 5-Year Penalty for Revealing Work Secrets

The Criminal Information Center (Wa'i) of the UAE's Public Prosecution recently brought attention to the consequences of sharing confidential company information on social media, with the undercurrent of "Work secrets are trust."

Dubai seized 1,274 drug shipments last year, including heroin, meth & marijuana

Dubai Customs reported 1,273 seizures of illicit drugs at land, sea, and air ports across the emirate as part of efforts commemorating the International Day Against Drug Abuse and Illicit Trafficking.

A new fuel prices in the UAE for the month of July.. Changes in taxi prices

The UAE has recently implemented new fuel tariffs for the month of July. The prices of taxis have been adjusted.

UAE Petrol Prices Decline Once More for July 2024

The UAE has announced a reduction in petrol prices for July 2024, marking the second consecutive month of price decreases across the country.

UAE Takes Action Against Counterfeit Goods with 620 Violations Recorded in 2023

Since the beginning of 2023 through the first half of the year, the UAE's Ministry of Economy has conducted 4,444 inspection tours across local markets. These efforts target cases of commercial fraud, imitation, and trademark counterfeiting,...

UAE Sets 6 New Rules from Fines to Paid Parking, Changes Effective July

As we approach the midpoint of 2024, the UAE has been abuzz with significant developments that are set to impact daily life and financial planning across the Emirates.

New fees and fines will be imposed on UAE residents starting July 1

There are six new restrictions that will take effect in July, ranging from paid parking to new fines in the UAE.

The UAE authorities announced the amendment of the system of paid parking fees in several areas

It was declared by the authorities in the UAE that they would be changing the system of paid parking fees in a number of different regions.

The UAE warns of hail and rain in some areas and issues an orange alert

This morning, the National Center of Meteorology in the United Arab Emirates issued an orange alert regarding the weather conditions in the UAE. The center warned of rain in some eastern regions, in addition to the presence of dusty conditions...

UAE police arrested Hundreds in overnight crackdown on cybercrime syndicates

In a sweeping overnight initiative across the UAE, significant cybercrime networks were disrupted, marking a pivotal moment in law enforcement's ongoing battle against digital crime.

UAE: Four New Mosques on Famous Square Corners Wow Residents

Sharjah has constructed four new mosques with traditional Islamic styles that really reflect Arab culture and Islam.

Dubai schools top global rankings in financial literacy and creative thinking

Dubai’s private schools have once again affirmed their global standing by achieving impressive rankings in financial literacy and creative thinking in the 2022 Programme for International Student Assessment (PISA), conducted by the Organisation for...

UAE: Ministry of Foreign Affairs issued a warning to travelers to 6 countries

The Ministry of Foreign Affairs of the United Arab Emirates issued a caution to travelers to six other nations.

Sharjah Summer Sale: 75% Discounts and Gold Prizes Starting July 1 in UAE

On July 1, Sharjah's much awaited massive summer sale returns promise for large bargains, spectacular events, and raffle prizes of Dh3 million.

Dubai clarifies process for residents to claim deposited funds from local hotels